{"id":48227,"date":"2024-01-26T13:43:10","date_gmt":"2024-01-26T16:43:10","guid":{"rendered":"https:\/\/academiadepacientes.com.br\/?p=48227"},"modified":"2026-02-18T12:32:44","modified_gmt":"2026-02-18T15:32:44","slug":"europa-retira-translarna-para-distrofia-muscular-de-duchenne","status":"publish","type":"post","link":"https:\/\/academiadepacientes.com.br\/?p=48227","title":{"rendered":"Europa Retira Translarna para Distrofia Muscular de Duchenne"},"content":{"rendered":"\n<p><strong>O que h\u00e1 de novo:<\/strong><br>\ud83d\udcc9 A PTC Therapeutics enfrenta um rev\u00e9s significativo com a retirada do Translarna\u00ae, seu medicamento para Distrofia Muscular de Duchenne (DMD), ap\u00f3s parecer negativo do regulador europeu.<\/p>\n\n\n\n<p><strong>Por que isso importa:<\/strong><br>\ud83c\udfe5 A decis\u00e3o impacta diretamente pacientes com DMD na Europa, que perdem uma op\u00e7\u00e3o de tratamento. \ud83d\udcb0 Tamb\u00e9m afeta as finan\u00e7as da PTC Therapeutics, com uma esperada redu\u00e7\u00e3o na receita de US$ 214 milh\u00f5es em 2024.<\/p>\n\n\n\n<p><strong>O quadro geral:<\/strong><\/p>\n\n\n\n<ol class=\"wp-block-list\">\n<li>Translarna recebeu aprova\u00e7\u00e3o condicional na Uni\u00e3o Europeia em 2014 para tratar DMD com &#8220;muta\u00e7\u00e3o sem sentido&#8221; em crian\u00e7as ambulatoriais com mais de cinco anos.<\/li>\n\n\n\n<li>O parecer negativo do Committee for Medicinal Products for Human Use (CHMP) leva \u00e0 retirada do medicamento, um golpe para pacientes com poucas op\u00e7\u00f5es de tratamento.<\/li>\n\n\n\n<li>DMD afeta cerca de um em cada 3.500 nascimentos masculinos globalmente, destacando a necessidade de tratamentos eficazes .<\/li>\n<\/ol>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<p>Fonte: <a href=\"https:\/\/br.tradingview.com\/news\/reuters.com,2024:newsml_L1N3EF34H:0\/\" title=\"\">Europa retirar\u00e1 medicamento para dist\u00farbios musculares raros da PTC Therapeutics<\/a><\/p>\n","protected":false},"excerpt":{"rendered":"<p>A decis\u00e3o impacta diretamente pacientes com DMD na Europa, que perdem uma op\u00e7\u00e3o de tratamento<\/p>\n","protected":false},"author":2,"featured_media":48228,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"om_disable_all_campaigns":false,"_uag_custom_page_level_css":"","_monsterinsights_skip_tracking":false,"_monsterinsights_sitenote_active":false,"_monsterinsights_sitenote_note":"","_monsterinsights_sitenote_category":0,"footnotes":""},"categories":[267,92],"tags":[],"class_list":["post-48227","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-arquivos-de-transicao","category-noticias","infinite-scroll-item","resize-featured-image"],"aioseo_notices":[],"uagb_featured_image_src":{"full":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:auto\/h:auto\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2024\/01\/translarna.png",1792,1024,false],"thumbnail":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:150\/h:150\/q:mauto\/rt:fill\/g:ce\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2024\/01\/translarna.png",150,150,true],"medium":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:300\/h:171\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2024\/01\/translarna.png",300,171,true],"medium_large":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:768\/h:439\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2024\/01\/translarna.png",768,439,true],"large":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:1024\/h:585\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2024\/01\/translarna.png",1024,585,true],"1536x1536":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:1536\/h:878\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2024\/01\/translarna.png",1536,878,true],"2048x2048":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:auto\/h:auto\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2024\/01\/translarna.png",1792,1024,false],"mailpoet_newsletter_max":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:auto\/h:auto\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2024\/01\/translarna.png",1320,754,false]},"uagb_author_info":{"display_name":"Cl\u00e1udio Cordovil","author_link":"https:\/\/academiadepacientes.com.br\/?author=2"},"uagb_comment_info":0,"uagb_excerpt":"A decis\u00e3o impacta diretamente pacientes com DMD na Europa, que perdem uma op\u00e7\u00e3o de tratamento","_links":{"self":[{"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/posts\/48227","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/users\/2"}],"replies":[{"embeddable":true,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=%2Fwp%2Fv2%2Fcomments&post=48227"}],"version-history":[{"count":3,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/posts\/48227\/revisions"}],"predecessor-version":[{"id":48236,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/posts\/48227\/revisions\/48236"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/media\/48228"}],"wp:attachment":[{"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=%2Fwp%2Fv2%2Fmedia&parent=48227"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=%2Fwp%2Fv2%2Fcategories&post=48227"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=%2Fwp%2Fv2%2Ftags&post=48227"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}