{"id":47300,"date":"2023-10-19T16:09:59","date_gmt":"2023-10-19T19:09:59","guid":{"rendered":"https:\/\/academiadepacientes.com.br\/?p=47300"},"modified":"2026-02-18T12:27:16","modified_gmt":"2026-02-18T15:27:16","slug":"icer-arsa-cel-para-leucodistrofia-e-custo-efetivo-a-preco-exorbitante","status":"publish","type":"post","link":"https:\/\/academiadepacientes.com.br\/?p=47300","title":{"rendered":"ICER: Arsa-Cel para leucodistrofia \u00e9 custo-efetivo a pre\u00e7o exorbitante"},"content":{"rendered":"\n<p><strong>O que h\u00e1 de novo:<\/strong> A valoriza\u00e7\u00e3o elevada de terapias gen\u00e9ticas ganha novo destaque com o caso do arsa-cel. \ud83e\uddec<\/p>\n\n\n\n<p><strong>Por que isso importa:<\/strong> Esta avalia\u00e7\u00e3o ressalta uma tend\u00eancia crescente na precifica\u00e7\u00e3o de terapias gen\u00e9ticas, mostrando um cen\u00e1rio onde os benef\u00edcios potenciais justificam valores que alcan\u00e7am milh\u00f5es de d\u00f3lares. \ud83d\udcb0<\/p>\n\n\n\n<p><strong>O quadro geral:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>A terapia gen\u00e9tica arsa-cel para leucodistrofia metacrom\u00e1tica (MLD) foi avaliada pelo Institute for Clinical and Economic Review (ICER), que sugere que o tratamento poderia ser considerado custoefetivo em um pre\u00e7o que varia entre 2,3 a 3,9 milh\u00f5es de d\u00f3lares, dependendo da dura\u00e7\u00e3o dos efeitos do tratamento . \ud83d\udcca<\/li>\n\n\n\n<li>A discuss\u00e3o em torno da precifica\u00e7\u00e3o desta terapia gen\u00e9tica ressurge em um contexto onde j\u00e1 foi observada resist\u00eancia, como na Europa, com um pre\u00e7o de tabela de quase 4 milh\u00f5es de d\u00f3lares por tratamento, mas ainda assim, a terapia parece estar ganhando cobertura acima da marca de um milh\u00e3o de d\u00f3lares . \ud83d\udcb5<\/li>\n\n\n\n<li>O arsa-cel, tamb\u00e9m conhecido como Libmeldy na Uni\u00e3o Europeia, tem mostrado benef\u00edcios significativos, especialmente em casos de DLM infantil tardia pr\u00e9-sintom\u00e1tica e DLM juvenil pr\u00e9-sintom\u00e1tica, conforme avaliado pelo ICER . \ud83d\udc66\ud83d\udc67<\/li>\n<\/ul>\n\n\n\n<h2 class=\"wp-block-heading\"><a href=\"https:\/\/academiadepacientes.com.br\/terapia-genetica-icer-dos-eua-apoia-precos-de-milhoes-de-dolares-para-tratamento-de-leucodistrofia\/\" target=\"_blank\" rel=\"noopener\" title=\"\">Clique aqui para saber mais!<\/a><\/h2>\n","protected":false},"excerpt":{"rendered":"<p>Terapia gen\u00e9tica para leucodistrofia \u00e9 avaliada pelo Institute for Clinical and Economic Review (ICER) como custoefetiva a pre\u00e7os entre US $ 2,3 a 3,9 milh\u00f5es.<\/p>\n","protected":false},"author":2,"featured_media":13699,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"om_disable_all_campaigns":false,"_uag_custom_page_level_css":"","_monsterinsights_skip_tracking":false,"_monsterinsights_sitenote_active":false,"_monsterinsights_sitenote_note":"","_monsterinsights_sitenote_category":0,"footnotes":""},"categories":[267,92],"tags":[],"class_list":["post-47300","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-arquivos-de-transicao","category-noticias","infinite-scroll-item","resize-featured-image"],"aioseo_notices":[],"uagb_featured_image_src":{"full":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:auto\/h:auto\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2021\/07\/negocios.jpg",1280,959,false],"thumbnail":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:150\/h:150\/q:mauto\/rt:fill\/g:ce\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2021\/07\/negocios.jpg",150,150,true],"medium":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:300\/h:225\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2021\/07\/negocios.jpg",300,225,true],"medium_large":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:768\/h:575\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2021\/07\/negocios.jpg",768,575,true],"large":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:1024\/h:767\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2021\/07\/negocios.jpg",1024,767,true],"1536x1536":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:auto\/h:auto\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2021\/07\/negocios.jpg",1280,959,false],"2048x2048":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:auto\/h:auto\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2021\/07\/negocios.jpg",1280,959,false],"mailpoet_newsletter_max":["https:\/\/mlzfzsux7b5d.i.optimole.com\/w:auto\/h:auto\/q:mauto\/f:best\/https:\/\/academiadepacientes.com.br\/wp-content\/uploads\/2021\/07\/negocios.jpg",1280,959,false]},"uagb_author_info":{"display_name":"Cl\u00e1udio Cordovil","author_link":"https:\/\/academiadepacientes.com.br\/?author=2"},"uagb_comment_info":0,"uagb_excerpt":"Terapia gen\u00e9tica para leucodistrofia \u00e9 avaliada pelo Institute for Clinical and Economic Review (ICER) como custoefetiva a pre\u00e7os entre US $ 2,3 a 3,9 milh\u00f5es.","_links":{"self":[{"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/posts\/47300","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/users\/2"}],"replies":[{"embeddable":true,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=%2Fwp%2Fv2%2Fcomments&post=47300"}],"version-history":[{"count":4,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/posts\/47300\/revisions"}],"predecessor-version":[{"id":47308,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/posts\/47300\/revisions\/47308"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=\/wp\/v2\/media\/13699"}],"wp:attachment":[{"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=%2Fwp%2Fv2%2Fmedia&parent=47300"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=%2Fwp%2Fv2%2Fcategories&post=47300"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/academiadepacientes.com.br\/index.php?rest_route=%2Fwp%2Fv2%2Ftags&post=47300"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}